Rare Diseases Weekly Roundup

Weekly Roundup: December 7, 2018

Informações:

Sinopsis

This week, the team discuss Novartis' AVXS-101 FDA application; the UK regulators' promise to review its HTA system under a new voluntary pricing and access scheme and clinical trial updates from bluebirdbio’s gene therapy LentiGlobin. Presenter: Joanna Fernandes Contributor: Aparna Krishnan